Expert Talks
The problem with self-awareness in PKU
In this video, Dr Cary Harding (Oregon Health & Science University, Portland, OR, USA)discusses how individuals with hyperphenylalaninemia are often unaware of neurocognitive impairments until they have been effectively treated. He reviews how neuropsychological outcomes have been assessed in pharmaceutical trials, the limitations of outcome measures that are determined by self-assessment, and the need for future studies to catalogue functional outcomes.
Time: 19:00
Veeva code: EU-MPRL-PKU-00081